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Gene therapy for the muscular dystrophies / Jeffrey S. Chamberlain.
- Format:
- Video
- Author/Creator:
- Chamberlain, Jeffrey S., speaker, author.
- Series:
- Henry Stewart talks. Biomedical & life sciences collection. Gene transfer and gene therapy.
- Henry Stewart talks. Biomedical & life sciences collection. Molecular genetics of human disease.
- Gene transfer and gene therapy, 2056-452X
- Molecular genetics of human disease, 2056-452X
- Language:
- English
- Subjects (All):
- Duchenne muscular dystrophy--Gene therapy.
- Duchenne muscular dystrophy.
- Duchenne muscular dystrophy--Genetic aspects.
- Gene therapy.
- Genetic vectors--Therapeutic use.
- Genetic vectors.
- Human molecular genetics.
- Medical genetics.
- Muscular dystrophy--Gene therapy.
- Muscular dystrophy.
- Muscular dystrophy--Genetic aspects.
- Genetic Therapy.
- Genetic Vectors.
- Muscular Dystrophies--genetics.
- Muscular Dystrophies--therapy.
- Muscular Dystrophy, Duchenne--genetics.
- Muscular Dystrophy, Duchenne--therapy.
- Medical Subjects:
- Genetic Therapy.
- Genetic Vectors.
- Muscular Dystrophies--genetics.
- Muscular Dystrophies--therapy.
- Muscular Dystrophy, Duchenne--genetics.
- Muscular Dystrophy, Duchenne--therapy.
- Genre:
- Video recordings.
- Physical Description:
- 1 online resource (1 streaming video file (66 min.)) : color, sound.
- polychrome
- Place of Publication:
- London : Henry Stewart Talks, 2014.
- System Details:
- Mode of access: World Wide Web.
- video file
- Contents:
- Contents: Introduction to the muscular dystrophies
- Duchenne muscular dystrophy (DMD)
- Dystrophin, the gene product of the DMD locus
- The molecular basis of DMD
- Strategies for the development of DMD therapies
- Adeno-associated viral (AAV) vectors and micro-dystrophins
- Scaling gene therapies to large animal models
- Exon skipping therapies.
- Notes:
- Animated audio-visual presentation with synchronized narration.
- Title from title frames.
- Publisher Number:
- 3809 Henry Stewart Talks
- Access Restriction:
- Restricted for use by site license.
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